disease-modifying – Page 2

Advances on many fronts in the battle against the protein that causes Huntington's disease

This fall sees exciting announcements from a number of companies focused on novel Huntingtin Lowering technologies, including Wave, PTC and Voyager

December 4, 2018

Media reports of a wonder drug for neurodegenerative diseases like Huntington's disease are overhyped

May 7, 2017

Work with genome editing techniques (zinc fingers and CRISPR) brings these tools closer to use in HD clinical trials

October 31, 2016

Major Announcement: First HD patients treated with gene silencing drugs

October 19, 2015

How will we know whether HD-lowering treatments are working? New advancements in the detection of mutant huntingtin.

May 18, 2015

Does a specific amino acid deficiency contribute to the development of HD?

April 21, 2014

A new study claims that high-dose creatine "slows the onset of Huntington Disease". How much hope and how much hype?

February 11, 2014

Prana Biotechnology has released data demonstrating their drug, PBT2, is effective in animal models of HD

January 14, 2013

Silencing the Huntingtin gene using ASO drugs reaches further, lasts longer and is safe. Human trial soon?

June 21, 2012

2 bits of good news for RNAi gene silencing in HD: it's safe over six months, and a way to treat bigger brain areas

January 24, 2012